Growth and Transformation - diagnosed 3-6 years

Clear all

Más allá de la distrofina

Esta sesión de la conferencia brinda información sobre las terapias emergentes más allá de la restauración de la distrofina, así como actualizaciones/anuncios de las empresas en este espacio.

Han Phan, MD

Director

Rare Disease Research, LLC

See more from same speaker

Mindy Cameron

Patient Advocacy Lead

Santhera Pharmaceuticals

See more from same speaker

Matthew Klein, M.D., M.S., FACS

Chief Operating Officer

PTC Therapeutics

See more from same speaker

Abby Bronson

Vice President, Patient Advocacy & External Innovation

Edgewise Therapeutics

See more from same speaker

Daniel Paulson, MD

Vice President of Clinical Development

Capricor Therapeutics

See more from same speaker

Video
Share this:
Spreading Wisdom - diagnosed 6+ yearsGrowth and Transformation - diagnosed 3-6 years

Next Generation Technology Panel

A brief overview of the rationale behind next generation technology, as well as presentations from the companies in this space. Moderated discussion included.

Erin Brubaker

Chief Operating Officer

Code Bio

See more from same speaker

Michael Kelly, PhD

Chief Scientific Advisor

CureDuchenne

See more from same speaker

Joe McIntosh, MD

Chief Medical Officer

Gennao Bio

See more from same speaker

Genine Winslow, MSc

CEO & President

Chameleon Biosciences

See more from same speaker

Video
Share this:
Beginning the Journey - diagnosed 0-3 yearsGrowth and Transformation - diagnosed 3-6 yearsSpreading Wisdom - diagnosed 6+ years

Panel de discusión: El impacto de Duchenne en la familia

Este panel discutirá los portadores genéticos de Duchenne, cómo comunicar el diagnóstico a otros y las experiencias con la planificación familiar.

Gloria Orozco

Presidenta, Coalición Latinoamericana DMD/DMB

Coalición Latinoamericana DMD/BMD

See more from same speaker

Graciela Méndez

Fundadora

Enlace Distrofia Muscular Duchenne Becker AC​

See more from same speaker

Sarah G. Seth, MPH, CGC

Consejera Genética Certificada

Hospital de Niños de San Antonio

See more from same speaker

Video
Share this:
Beginning the Journey - diagnosed 0-3 yearsGrowth and Transformation - diagnosed 3-6 yearsSpreading Wisdom - diagnosed 6+ years

Pilares del viaje de transición

Esta sesión está destinada a familias/cuidadores de adolescentes y adultos con Duchenne. Cubre cuatro pilares del viaje transicional de Duchenne: Continuidad de la atención, Planificación del estilo de vida, Éxito financiero y Escuela/Carrera/Pasatiempos, y es seguido por una sesión de discusión/Preguntas y respuestas.

Pradeep P.A. Mammen, MD, FACC, FAHA

Associate Professor of Medicine and Co-Director

Senator Paul D. Wellstone Muscular Dystrophy Cooperative Research Center, Director for Translational Research for the Advanced Heart Failure and Transplant Cardiology Program, UT Southwestern Medical Center

See more from same speaker

Kent Williams, MD

Pediatric Gastroenterologist

Nationwide Children's Hospital

See more from same speaker

Jennifer Shumsky, BSN, RN, CHCO, PACS

Director, Payer Relations

Little Hercules Foundation

See more from same speaker

Hawken Miller

Journalist

Washington Post

See more from same speaker

Video
Share this:
Growth and Transformation - diagnosed 3-6 years

Pillars of the Early Journey

This session is intended for families/caregivers of children and adolescents with Duchenne. It covers four pillars of the early Duchenne journey: Multidisciplinary Care, Steroids, Nutrition, and Involvement in Clinical Trials, and is followed by a discussion/Q&A session.

Barry Byrne, MD, PhD

Professor and Associate Chair

University of Florida, Department of Pediatrics

See more from same speaker

Diana Castro, MD

Associate Professor of Pediatrics, Neurology and Neurotherapeutics

University of Texas Southwestern

See more from same speaker

Kindann Fawcett, PhD

Post Doctoral Fellow

University of Arkansas for Medical Sciences

See more from same speaker

Video
Share this:
Beginning the Journey - diagnosed 0-3 yearsGrowth and Transformation - diagnosed 3-6 years