Este panel discutirá los portadores genéticos de Duchenne, cómo comunicar el diagnóstico a otros y las experiencias con la planificación familiar.
Presidenta, Coalición Latinoamericana DMD/DMB
Coalición Latinoamericana DMD/BMD
Consejera Genética Certificada
Hospital de Niños de San Antonio
This session is intended for families/caregivers of teens and adults with Duchenne. It covers four pillars of the transitional Duchenne journey: Continuity of Care, GI-related Care, Medical Privacy, and School/Career/Hobbies, and is followed by a discussion/Q&A session.
Associate Professor of Medicine and Co-Director
Senator Paul D. Wellstone Muscular Dystrophy Cooperative Research Center, Director for Translational Research for the Advanced Heart Failure and Transplant Cardiology Program, UT Southwestern Medical Center
Director, Payer Relations
Little Hercules Foundation
Pediatric Gastroenterologist
Nationwide Children's Hospital
PTC Industry Presentation
Senior Medical Science Liaison, Medical Affairs
PTC Therapeutics
Este recurso proporciona información sobre las actividades en la piscina y las rutinas de estiramiento adecuadas.
RGX-202: REGENXBIO’s investigational gene therapy for the treatment of Duchenne Muscular Dystrophy presented by: Johannaz (Naz) Dastgir, DO, Senior Director, Clinical Development Lead at REGENXBIO
A program update on RGX-202, REGENXBIO’s investigational gene therapy program for the treatment of Duchenne.
Contact: Duchenne@regenxbio.com or patientadvocacy@regenxbio.com
Senior Director, Clinical Development Lead
REGENXBIO
Santhera Industry Presentation
Global Program Lead and Head of Medical Affairs
Santhera Pharmaceuticals
Sarepta Pipeline Update for the Duchenne Community
Contact Information for Patient Affairs Team: advocacy@sarepta.com
Our CureDuchenne Certified Physical Therapists talk about appropriate exercise for all mobility levels.
CureDuchenne Certified Physical Therapist
CureDuchenne Physical Therapy Program
Our CureDuchenne Certified Physical Therapists demonstrate at-home stretching techniques.
