Several years ago, soon after our son, Hawken’s diagnosis of Duchenne, I was at a conference, and full of mutation envy. Our son has a deletion of exon 45 and […]

Tyler Armstrong, 10, will be climbing Mt. Adams as a training climb in preparation for reaching the Seven Summits. Tyler has already climbed two of the Seven Summits – Mt. Kilimanjaro and […]

CureDuchenne is pleased to launch the 79 Days of Duchenne project with Sarah Burgess, singer-songwriter and contestant on the sixth season of American Idol. More than 79 talented individuals created […]

      Leiden, The Netherlands, June 25, 2014 (GLOBE NEWSWIRE) — Prosensa Holding N.V. (NASDAQ: RNA), the Dutch biopharmaceutical company focusing on RNA-modulating therapeutics for rare diseases with high […]

      CureDuchenne, a nonprofit that raises awareness and funds research to find a cure for Duchenne muscular dystrophy, issued the following statement today regarding the announcement by Prosensa […]

PTC Therapeutics announced this morning that they have received a positive opinion from the Committee for Medicinal Products for Human Use (CHMP) of the European Medicines Agency, regarding the company’s […]

      Dear Patient Group Representative,   We trust this letter finds you well. As announced in a press release and during our quarterly update for the financial community […]

  Sarepta Therapeutics, Inc. will host a webcast and conference call for the Duchenne muscular dystrophy (DMD) community on Tuesday, May 13, 2014, beginning at 11:00 am EDT (8:00 am […]

Re-dosing plans are underway and 96-week data from an open-label extension study of drisapersen for the treatment of DMD presented at the American Academy of Neurology (AAN) Leiden, The Netherlands, […]