EDO platform demonstrates potentially best-in-class safety and efficacy profile in addressing DMD and DM1 disease phenotypes Advancing rapidly to the clinic with first-in-human studies expected to initiate in early 2022 […]
This presentation by Kimberly Nugent, CGC at Children’s Hospital of San Antonio is part of The Family Unit webinar and covers the following topics: genetic carrier health, carrier testing options […]
This webinar is a roundtable with scientific and medical experts covering recent updates to COVID-19 vaccines and how they relate to the Duchenne community. You’ll be prompted to enter your […]
Pratteln, Switzerland, March 3, 2021 – Santhera Pharmaceuticals (SIX: SANN) announces that the last patient has completed the last visit for the first period of the placebo-controlled pivotal VISION-DMD study with […]
In this webinar, Sarepta Therapeutics discusses their commitment to individuals living with Duchenne and the community. They provide an overview of their RNA Exon-Skipping therapies as well as Sarepta’s patient […]
This webinar covers the following topics: Co-parenting/caregiving, Marriage and Communication Genetic Carrier Health Ask the Expert Session You’ll be prompted to enter your name and email address to view the […]
************** Join CureDuchenne and Sarepta on March 4 for a webinar discussing the below announcement. CureDuchenne Webinar: Sarepta Therapeutics update on RNA Exon-Skipping program and Patient Support Services In this […]
Dear Duchenne Community, All of us at Italfarmaco would like to thank the families participating in the Phase 3 EPIDYS trial and in the open label extension study of givinostat […]
Meet the leaders at Edgewise Therapeutics and hear their company goals related to treatments for Duchenne muscular dystrophy. You’ll be prompted to enter your name and email address to view […]
