Learn about PTC Cares™, a support program dedicated to helping patients, caregivers, and prescribers understand the prescription process, financial assistance, and insurance information for PTC products. You’ll be prompted to […]
-Collaboration combines Solid’s differentiated microdystrophin construct and Ultragenyx’s HeLa PCL manufacturing platform for use with AAV8 and variants- -Solid receives $40 million upfront via equity investment at a premium; up […]
The CureDuchenne Time Capsule Video is a beautiful compilation of interviews conducted at the 2019 FUTURES Conference in Anaheim, CA. We asked families to share their stories with us, as […]
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Dear Duchenne community, Since 2016, Santhera has been conducting one of the largest clinical trials in Duchenne muscular dystrophy – the SIDEROS study. SIDEROS is a phase III double-blind, randomized, […]
La 2da parte incluirá los siguientes temas: Educación para el cuidador Sugerencias para los cuidadores – mejores prácticas físicas, mentales y emocionales Anécdota familia & construcción comunitaria Se le pedirá […]
La 1ra parte incluira los siguientes temas: Acceso al Cuidado Multidisciplinario Guia nutricional para Individuos con Duchenne Programa de Asistencia Familiar Duchenne (Duchenne Family Assistance Program) Se le pedirá que […]
This month’s Catabasis Connection:
Dear U.S. Duchenne community, As you know from our previous updates, the SIDEROS clinical trial is fully enrolled and Santhera has been working with the Food and Drug Administration (FDA) […]
