This webinar, in partnership with the University of Kansas Medical Center, explores topics like achieving milestones, quality of life, and setting goals in families navigating Duchenne muscular dystrophy. The panelists […]
Children and adults with complex neuromuscular disorders such as Duchenne muscular dystrophy depend on others for controlling their environment, their mobility and most daily living activities. There are new technologies […]
Currently, there is a clear paucity of information to guide exercise prescription for patients with DMD. While clinical concerns based on the notion that excessive exercise may exacerbate the disease […]
Join us for a presentation on the clinical development process behind approved therapies and the importance of dose and administration of corticosteroids by Dr. Emma Ciafaloni. This presentation will be […]
This presentation by Lauren Morgenroth, CGC and Ana Christensen, MPH at TRiNDS is part of the “A Holistic View of Clinical Trials” webinar and covers the following topics: the clinical […]
Webinar Information PepGen presents an overview of its enhanced delivery oligonucleotide platform and how this innovative platform technology is being applied to create a transformative exon skipping therapy. James McArthur, […]
This webinar covers the following topics: Understanding the Clinical Trial Process Managing Expectations Featured Speakers: Ana Christensen, MPH – TRiNDS and Italfarmaco Leslie Porter – Family, Duchenne Advocate Michael Kelly, […]
What is the role of exercise in patients with Duchenne Muscular Dystrophy? Special guest, Dr. Aaron S. Zelikovich, MD Original Webinar date: February 23, 2021Please submit your questions or comments […]
Enhancing Muscle Delivery of ASOs to treat Duchenne Dyne is excited to present an overview of their FORCETM platform and DMD drug development program to the Duchenne community and then […]